A new method for safely inserting large chunks of DNA into genomes has now measured up in mice, potentially paving the way ...

After teasing a new regulatory process for personalized genetic medicines at the end of last year, the FDA today unveiled draft guidance for an approval pathway that could see custom CRISPR therapies, ...

Rapid advancements in CRISPR and next-generation gene editing technologies, combined with a strong clinical pipeline ...

Growing Adoption of Gene Therapy Platforms, Expanding Agricultural Biotechnology Applications, and Accelerating Clinical Trial Activity Drive Robust Market Expansion.Austin, United States, Feb. 27, ...

Gene therapy and genome editing are promising for treating glycogen storage disease (GSD), especially Pompe disease and von Gierke disease. Pompe disease results from acid α-glucosidase (GAA) ...

The U.S. Food and Drug Administration approved the first cell-based gene therapies for sickle cell disease, including the ...

In a historic medical breakthrough, a child diagnosed with a rare genetic disorder has been successfully treated with a customized CRISPR gene editing therapy by a team at Children's Hospital of ...

Powered by gene editing advances like CRISPR and base editing, cell and gene therapy (CGT) is delivering on the promise of genomic medicine. First-generation CAR T-cell therapies, for example, have ...

UCLA researchers use lipid nanoparticles to insert full CFTR gene into airway cells, restoring function and opening new avenues for CF therapy.

The 28th American Society of Gene & Cell Therapy (ASGCT) meeting kicks off in mid-May in New Orleans. The annual event, which is on pace toward a goal of 8,000 attendees, will be a whirlwind of ...

Bionano Symposium 2026 continues with Day 3: OGM Making its Mark in Constitutional Genetic Disorders on February 25, 2026, from 7:00-10:00 AM PT. Attendees may also explore scientific posters ...